The webinar will feature presentations from Key Opinion Leaders (KOL’s)

Barbara Burton, M.D., Professor of Pediatrics, Northwestern University Feinberg School of Medicine, and Attending Physician in the Division of Genetics, Birth Defects and Metabolism at the Ann & Robert H. Lurie Children’s Hospital of Chicago, will provide an overview of Arginase 1 Deficiency and describe the role of arginine in the pathogenesis of the disease.

George Diaz, M.D., Ph.D., Professor of Genetics and Genomic Sciences, Icahn School of Medicine, and Director of the Program for Inherited Metabolic Diseases at Mount Sinai (New York, NY), will discuss the enzyme therapy approach to treating patients with Arginase 1 Deficiency and clinical data.

Tanja Brandt, parent/caregiver of a 10-year old child with ARG1-D, Advisor and Steering Committee Member of the Arginase 1 Deficiency Foundation (ARG1D.org), will discuss the disease burden and will provide the patient and caregiver perspective related to the challenges of living with a devastating and progressive disease.

A live question and answer session will follow.