Arrowhead Pharmaceuticals Summer Series of R&D Webinars – Part I: ARO-DM1 in Type 1 Myotonic Dystrophy and ARO-DUX4 in Facioscapulohumeral Muscular Dystrophy
DATE: | May 23, 2024 |
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TIME: | 2:00 PM EDT |
LOCATION: | Virtual |
About The Event
Join Arrowhead Pharmaceuticals for Part I of its Summer Series of R&D webinars, featuring Lawrence Korngut, MD (University of Calgary Cumming School of Medicine) and company management, who will discuss the following Targeted RNAi Molecule (TRiMTM) platform-derived development programs:
- ARO-DM1, an RNAi conjugate designed to specifically silence DMPK mRNA in skeletal muscle, currently being evaluated in Phase 1/2a dose-escalating study in patients with type 1 myotonic dystrophy
- ARO-DUX4, an RNAi conjugate designed to specifically target the gene that encodes human double homeobox 4 (DUX4) protein, currently being evaluated in Phase 1/2a dose-escalating study in adult patients with facioscapulohumeral muscular dystrophy (FSHD)
A live question and answer will follow the formal presentations.